Lantern Pharma, Georgetown University partner on prostate cancer drug
October 5, 2020 -- Lantern Pharma is extending its collaboration with Georgetown University for LP-184, a small molecule drug candidate, currently in preclinical development for certain genomically defined solid tumors including prostate and pancreatic cancers.
BioMarin receives fast track designation for PKU gene therapy
October 2, 2020 -- The U.S. Food and Drug Administration has granted BioMarin Pharmaceutical fast track designation for BMN 307, an investigational gene therapy drug for the treatment of individuals with phenylketonuria (PKU).
Bluebird Bio gets gene therapy EMA marketing nod accepted
October 2, 2020 -- The European Medicines Agency (EMA) accepted Bluebird Bio's marketing authorization application for its investigational elivaldogene autotemcel gene therapy drug to treat patients with cerebral adrenoleukodystrophy.
Ionis, Genuity Science partner to advance RNA-targeted therapies
October 1, 2020 -- Ionis Pharmaceuticals and Genuity Science have entered a multiyear collaboration to accelerate the discovery and development of genetically validated targets for up to 20 diseases.
CRB introduces multimodal facility to support cell & gene therapy clients
September 30, 2020 -- CRB has created SlateXpace, a multimodal manufacturing facility solution to support complex therapeutic product pipelines.
Regenxbio expands clinical development for Hunter syndrome gene therapy
September 30, 2020 -- Regenxbio has expanded its RGX-121 gene therapy program for the treatment of mucopolysaccharidosis type II (Hunter syndrome) to evaluate the product in a broader patient population.
Bio-Techne opens GMP manufacturing facility
September 30, 2020 -- Bio-Techne has opened a 61,000-sq-ft good manufacturing practice (GMP) manufacturing facility in St. Paul, MN. The space will be dedicated to large-scale production of Escherichia coli-derived recombinant proteins for cell and gene-modified therapy workflows.
Irvine Scientific to exclusively distribute stem cell tech
September 29, 2020 -- Fujifilm Irvine Scientific said it has become the exclusive worldwide distributor of cellnest, a recombinant peptide attachment substrate that's designed to provide optimal adhesion and proliferation of stem cells for cell and gene therapy research.
Bioray Labs develops nonviral targeted CAR T therapy
September 28, 2020 -- Bioray Laboratories posted interim results from clinical trials of its nonviral programmed cell death 1 specific targeted chimeric antigen receptor (CAR) T therapy for relapsed/refractory B-cell non-Hodgkin lymphoma.
Avrobio gets orphan drug nod for Gaucher disease gene therapy
September 28, 2020 -- Avrobio has been granted orphan drug designation for AVR-RD-02, an investigational gene therapy for treatment of Gaucher disease, by the European Commission.
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