Foundation, medical schools partner on gene therapy for H-ABC
October 13, 2020 -- The nonprofit organization Foundation to Fight H-ABC has signed an agreement with the University of Massachusetts Medical School and Yale University to sponsor research aimed at using gene therapy to treat hypomyelination with atrophy of the basal ganglia and cerebellum (H-ABC), a rare degenerative children's disease.
Survey queries informed consent for genome editing clinical trials
October 13, 2020 -- A new survey asked sickle cell disease patients, their parents, and physicians about what they want and need to know about genome editing in order to make an informed decision to participate in a clinical trial.
Targovax granted European patent for cancer immunotherapy
October 12, 2020 -- The European Patent Office has granted a patent to clinical stage immuno-oncology firm Targovax for use of its modified adenovirus in combination with checkpoint inhibitors for cancer therapeutics.
Moderna secures $56M for mobile vaccine manufacturing
October 8, 2020 -- Moderna has received $56 million from the Defense Advanced Research Projects Agency to fund manufacturing of nucleic acid vaccines and therapeutics.
TreeFrog, Invetech partner on automated single-use stem cell encapsulation
October 8, 2020 -- TreeFrog Therapeutics and Invetech have entered a strategic partnership to develop a good manufacturing practices-compliant device for high-throughput stem cell encapsulation by the end of 2022.
Swift Biosciences debuts new DNA library kit
October 7, 2020 -- Swift Biosciences has launched Swift 2S Sonic DNA library kit for low-cost enzymatic fragmentation-based library preparation. The kit is compatible with mechanically fragmented double-stranded DNA to support next-generation sequencing applications.
Synthego introduces new CRISPR light control tech
October 7, 2020 -- Synthego has designed a new foundational technology for standardized precision and control of CRISPR-based genome editing inside cells using light.
Unchained Labs launches new gene therapy tool
October 6, 2020 -- Unchained Labs has launched a new gene therapy quantification application on Stunner, its gene therapy platform.
Diamond Pharma, GenSight submit EMA application for ocular gene therapy
October 6, 2020 -- French biotechnology firm GenSight Biologics has submitted a marketing authorization application to the European Medicines Agency (EMA) for its ocular gene therapy.
Avrobio expands Hunter syndrome gene therapy program
October 6, 2020 -- Avrobio has signed a research and licensing agreement with the University of Manchester in the U.K. to investigate the use of lentiviral gene therapy for mucopolysaccharidosis type II, aka Hunter syndrome.
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