Through the collaboration, Lysogene and Anthony Futerman, PhD, of the Weizmann Institute will work to develop a novel adeno-associated virus (AAV) gene therapy approach for neuronopathic Gaucher disease, Parkinson's disease, and other diseases associated with mutations of the GBA1 gene.

Under the terms of the agreement, Lysogene will provide expertise in AAV vector design and production, while Futerman's lab will provide glucocerebrosidase variants with enhanced biological properties and conduct proof-of-concept biological studies. Subsequently, Lysogene will have the option to license the program.

Novasep, Lysogene partner for gene therapy
Novasep and Lysogene announced that the parties have inked an agreement for the development and manufacturing of an adeno-associated viral vector-based...